CURE GM1 RUN WALK CHALLENGE - RUN AND WALK FOR THOSE WHO CAN'T!
http://curegm1.org/run_walk_challenge/ During the entire month of September 2017 we are challenging everyone to Run and Walk for a child with GM1 Gangliosidosis, and then donate in their name. See the link above for all challenge information and links on where to buy T-shirts. Thank you for making a difference for children with GM1 Gangliosidosis.
The Cure GM1 Foundation is dedicated to hope and to directly funding research for a cure for GM1 Gangliosidosis, a lysosomal storage disease that attacks the brain and spinal cord and is always fatal in children.
GM1 is a progressive and degenerative condition with an extremely broad and debilitating array of symptoms and complications. This nonprofit organization was founded by parents of children who suffer from GM1 who seek to save the lives of all those who suffer from this wretched condition. With the generous support of GM1 families, those affected by GM1, and the support of the world, we believe a cure can be found. Research is advancing on multiple fronts globally. These efforts require financial support.
Areas of research include:
- Lentiviral gene therapy
- Small molecules
- Chaperones Substrate Reduction Therapies
- Enzyme replacement therapy
- AAV gene therapy