Abby is our 10 year old daughter and was diagnosed with a rare, terminal disorder known as Sanfilippo Syndrome Type A.
There is currently no cure or treatment.
There is promising research in Gene Therapy at Nationwide Children's Hospital in Ohio, however funds for the trials are lacking and need our support. We are focusing our fundraising efforts on joining other Sanfilippo Syndrome foundations to support the Gene Therapy Clinical Trials that are planned to start in 2015. This is our chance to find a cure for Abby and save her life!
Please buy a glass for Abby & her friends so we can fund the cure and toast to their long life! Thank you.