The Shepherd's Gift: GM1 for HD
Team Member: Susan Holler
We have worked for over 2 decdes to bring ovine GM1 to a clinical trial. The potential it has to improve the quality of life for those who struggle with devastating neurologic diseases keeps us working to get it approved for human pharmaceutical use. As we have gotten to know families who live with HD we are more dediicated than ever to get it approved. The courage and faith of these families is inspirational. The FDA pre-IND approval of the sheep source for GM1 ganglioside production was necessary for us to have a chance with the NIH/NINDS CREATE grant submission. Hopefully this funding will keep us moving forward. Unfortunately, without some type of outside investment, the pace will be much slower. You can help by supporting this crowdrise grassroots effort to improve the quality of life for HD families. In Isaiah 40,verse 31, we are told, “But those who trust in the Lord will find new strength. They will soar high on wings like eagles. They will run and not grow weary. They will walk and not faint”. The path forward to the clinic is laid out right in front of us. It’s just gonna be one step at a time. All we have to do is trust.